A recent study on gene therapy for Danon disease revealed findings related to its impact on the condition’s hallmark cardiac pathology. What finding suggested the therapy could effectively target the...
Danon disease is a rare genetic disorder with three distinct characteristics that affect boys more severely than girls. Can you correctly identify the three main features of Danon disease? Take the quiz to...
A 2-year-old boy presents with his parents to a pediatric clinic. He had previously been diagnosed with hypospadias. His parents explain that he has been showing symptoms of troubled breathing, excessive...
